Precision gene editing could prevent vision loss from Stargardt disease
Researchers have developed a therapy to treat Stargardt disease, the most common form of inherited macular degeneration, ...
GEN13d
Base Editing Addresses Inherited Macular Degeneration in Primate, Human Tissue Models
A collaboration between scientists at the Institute of Molecular and Clinical Ophthalmology Basel (IOB) and Beam Therapeutics has resulted in a new base editing therapy for Stargardt disease ...
The Globe and Mail1mon
Stargardt Disease Therapeutics Market Size in the 7MM was ~USD 27 million in 2023, which is expected to increase by 2034, estimated DelveInsight
DelveInsight’s “Stargardt Disease Market Insights, Epidemiology, and Market Forecast-2034″ report offers an in-depth understanding of the Stargardt Disease, historical and forecasted ...
Yahoo Finance1mon
FDA clears SpliceBio’s IND application to begin Stargardt disease therapy trial
SpliceBio CEO and co-founder Miquel Vila-Perelló said: “The FDA IND clearance of SB-007 is a significant achievement for SpliceBio and Stargardt disease patients. As the first-ever IND for a ...
manilatimes2mon
Alkeus Pharmaceuticals Receives FDA Rare Pediatric Disease and Fast Track Designations for Gildeuretinol as a Treatment for Stargardt Disease
Designations underscore significant unmet need in Stargardt disease, a rare and serious pediatric disease for which no treatment exists. Data from Alkeus' TEASE program were presented at the American ...