Genome editing ... gene editing – both because the field is pushing medicine into areas we might never have dreamed possible, and because these technologies involve literally cutting DNA at a ...
Researchers at ShapeTX have developed a platform to generate viral vectors that target specific tissues ... gene therapies. ShapeTX is already working in partnership with Roche to advance RNA ...
SPLICER builds upon the popular CRISPR-Cas9 gene editing platform — with key changes. CRISPR-Cas9 systems require a specific DNA sequence to latch on, limiting which genes could be edited.
Further studies could focus on patient-derived organoids to study gene function in tissue and disease-specific contexts. "We ...
To address these challenges, researchers are developing novel viral vector designs, such as self-inactivating vectors, tissue-specific promoters, and targeted gene editing approaches. Additionally, ...
Intellia is working to develop the gene editing therapy being delivered. Intellia’s therapy is designed to target permanent or near-permanent correction of a specific nonsense mutation (also ...
With AI taking more and more space in biotech, CRISPR stands out as one of the most promising avenues for AI integration.
VLPs offer efficient transduction, tissue tropisms, reduced off-target editing, and transient cargo expression. Previously, the current study's authors developed eVLPs that enable efficient gene ...
In vivo refers to studies or experiments conducted on living organisms or cells instead of dead organisms or tissue extracts ... achieved high-efficiency gene editing in non-human primates ...
--(BUSINESS WIRE)--ReCode Therapeutics, a clinical-stage genetic medicines company using tissue-specific delivery ... s proprietary CRISPR-based gene editing platform, including its DNA-writing ...
The resulting toolkit will allow CRISPR gene editing to be precisely targeted to the specific areas requiring ... of tumor cells without harming healthy tissue. The latest work also uses cancer ...